Rare doesn’t mean small. More than 30 million people in the U.S. and 400 million worldwide live with a rare disease—yet 90% still have no FDA-approved treatments. We're honored to support Emily's Entourage and their commitment to leading the charge to redefine what's possible for rare diseases, especially the final 10% of people living with #CysticFibrosis. We strive to continually innovate to realize the full potential of transformative #GeneticMedicines for those in need. #ExtraordinRARE #RareDiseaseDay #RareDiseaseWeek
Thank you for your incredible support and commitment to transforming the future for the final 10% of people with CF and the rare disease community! 💜
Студент(ка) в уч. заведении EPMH
1moPlease tell me, is there still no news? 4D-710 in Cystic Fibrosis (AEROW Study)